1. United States
2. Pa.
3. Letter

I have a friend who has been on elamipretide for three years -- the only treatment that has made a meaningful difference in her life with primary mitochondrial myopathy—a degenerative genetic condition that impairs how her cells convert food and oxygen into energy. Mitochondria provide over 90 percent of the energy our bodies need; when they fail, the highest-demand tissues—like muscle, brain, and heart—are hit the hardest. For her, that has meant profound fatigue, muscle weakness, shortness of breath, double vision, and severely reduced stamina. There is no approved disease-modifying treatment—only supportive care. The disease is terminal, and until now, no therapy has reached this point in offering real potential to change its course. BUT the FDA is about to make a critical decision that could cut off elamipretide. CONGRESS MUST STOP THIS AND OTHER CUTS TO SCIENCE AND MEDICINE!!! Too many people rely on REAL modern medicine to let RFK jr run roughshod over science.